XVIII OGÓLNOPOLSKI TYDZIEŃ MUKOWISCYDOZY 25.02 – 03.03.2019 FUNDACJA „MATIO” Działania podejmowane w trakcie XVIII Ogólnopolskiego Tygodnia Mukowiscydozy Bezpłatne badania genetyczne prowadzone przez Centrum Medyczne MED-GEN Akcja edukacyjna w Galerii Bronowice w Krakowie we współpracy
Vertex Pharmaceuticals ogłosił, że Amerykańska Agencja ds. Żywności i Leków (FDA) zatwierdziła Symdeko (tezacaftor / iwakaftor i iwakaftor) jako terapię dla pacjentów z mukowiscydozą (CF) niosących dwie kopie mutacji F508del w genie CFTR (gen defektywny w CF) lub z jedną
Two of Proteostasis’ Three Cystic Fibrosis Therapies Are in Clinical Trials, and the Third Is Heading for TrialsTwo of the three therapies that Proteostasis Therapeutics has developed to correct the
New Vertex drugs show dramatic gains for tough-to-treat cystic fibrosis patients By ADAM FEUERSTEIN @adamfeuerstein Vertex Pharmaceuticals scored a major win Tuesday with the release of data from three clinical trials
Nowa terapia genowa. Czy będzie nadzieją dla nieuleczalnie chorych? Piątek, 17 listopada (10:33) To może być przełom w leczeniu wielu chorób genetycznych. Lekarze z Kalifornii podjęli się pierwszej na świecie
New Data Supports SPX-101 as Potential Future Therapy for CF Patients MAY 30, 2017
FDA Approves KALYDECO® (ivacaftor) for More Than 900 People Ages 2 and Older with Cystic Fibrosis Who Have Certain Residual Function Mutations – Precision medicine decision based on in vitro
Mutated mice that inhaled SPX-101 lived longer, according to a new preclinical study that highlights the drug’s potential to clear mucus and hydrate airways in patients with cystic fibrosis (CF). The study,
Scientists at Boston University’s Center for Regenerative Medicine have made two stem cell discoveries that could help doctors treat cystic fibrosis (CF) without having to resort to transplants. They prevented stem
Potential new treatment to treat and stop progression of cystic fibrosis April 10, 2017 Source: George Washington University Summary: Researchers have discovered a potential new drug to treat and stop
Nie znasz języka angielskiego, już nie musisz – Combined Tezacaftor, Kalydeco Therapy Significantly Improved CF Lung Function in Clinical Trials APRIL 3, 2017 BY PATRICIA INACIO, PHD IN CYSTIC FIBROSIS,
The World Health Organisation (WHO) has published a list of the 12 bacteria which pose the greatest threat to human health because they are resistant to antibiotics. Health experts have
Potentially Dangerous Bacterial Infection May Be Common in CF, But Few Show Symptoms JANUARY 17, 2017 BY MAGDALENA KEGEL IN NEWS. The bacterial species Clostridium difficile is often found in